New Research Suggests Gene Therapy Could Be Used To Treat Pitt-Hopkins Syndrome

Postnatal gene therapy may be able to prevent or repair many of the harmful effects of Pitt-Hopkins syndrome, a rare genetic condition, according to researchers at the University of North Carolina School of Medicine. In an animal model of Pitt-Hopkins syndrome, researchers discovered that restoring lost gene activity eliminates numerous clinical indications. https://gadgets360.com/science/news/gene-therapy-could-treat-pitt-hopkins-syndrome-new-research-suggests-3041858#rss-gadgets-science